The FDA has accepted PTC Therapeutics' NDA for vatiquinone, a potential treatment for Friedreich's ataxia, with a decision expected by August 19, 2025. PTC Therapeutics has announced that the FDA has ...

Sanjiv Harpavat, MD, PhD, FAAP, lead author of a clinical report recently released by the AAP on identifying infants with biliary atresia, joined to discuss the report and guidance for primary care. A ...

Infant mortality rates increased in US states with abortion bans, reversing previous declines. States with bans saw 478 excess infant deaths, with the highest increases in Texas and Kentucky. Black ...

90-day interim biopsy data in the first 3 patients revealed an average microdystrophin expression of 110% and improvements in muscle health and resilience biomarkers. Positive initial data has been ...

0.05% atropine was associated with a higher incidence of mild side effects, though it was more effective in controlling myopia progression compared to 0.01% atropine or placebo. A new study published ...

In this quiz, we test your knowledge of the AAP's new algorithm and updated recommendations for newborn screening for critical congenital heart disease. In December 2024, the American Academy of ...

Panelists discuss the prevalence of treatment-refractory moderate to severe atopic dermatitis, noting factors such as intolerance or inability to use high-potency topical agents as common reasons for ...

A study found that teens with obesity eat more later in the day than their peers, highlighting the role of the body’s circadian system in eating habits. A new study from researchers at Mass General ...

Panelists discuss treatment expectations for newer systemic agents, highlighting data on efficacy onset and persistence, including rapid improvement in pruritus with dupilumab by week 2 (SOLO trials), ...

Nurse practitioner Donna Hallas, PhD, PPCNP-BC, CPNP, PMHS, FAANP, FAAN offers her thoughts on the recent FDA approval of GSK's meningococcal ABCWY vaccine. On February 14, 2025, the FDA approved ...

The combination vaccine targets 5 groups of the bacteria Neisseria meningitidis (A,B,C,W, AND Y) that cause the most invasive meningococcal disease cases (IMD) globally. The FDA has approved ...

The federal agency has approved Merilog (insulin-aspart-szjj) as biosimilar to Novolog (insulin aspart) for the improvement of glycemic control in adults and pediatric patients with diabetes mellitus.